May. 13 at 2:58 AM
$CAPR
After Deramiocel is approved for DMD in the US, and the marketing issue is solved...what is next? Linda said...
"Our first target will likely be expansion to the younger DMD patients we are working on now. In addition, we plan to initiate the clinical pathway for Becker muscular dystrophy, which we plan to begin discussing with the FDA immediately following PDUFA for DMD. Expansion of deramiocel outside the United States is also underway, and we expect to meet with the EMA and PMDA later this year. We believe deramiocel should be available to all patients worldwide, and that will be a goal that we actively work towards this year. In addition, we're evaluating opportunities in other rare neuromuscular diseases where inflammation and fibrosis are the primary pathologies."
Look to partnering with Big Pharma to reach "patients worldwide" and StealthX exosome therapeutics enter the clinic next year!